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Gait Event Detection and Travel Distance Using Waist-Worn Accelerometers across a Range of Speeds: Automated Approach. Sensors (Basel). 2024 Feb 09; 24(4).
Ramli AA, Liu X, Berndt K, Chuah CN, Goude E, Kaethler LB, Lopez A, Nicorici A, Owens C, Rodriguez D, Wang J, Aranki D, McDonald CM, Henricson EK. PMID: 38400313; PMCID: PMC10891633.
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PubMed Mentions:
1 Fields:
Translation:
Humans
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Gait Characterization in Duchenne Muscular Dystrophy (DMD) Using a Single-Sensor Accelerometer: Classical Machine Learning and Deep Learning Approaches. Sensors (Basel). 2024 Feb 08; 24(4).
Ramli AA, Liu X, Berndt K, Goude E, Hou J, Kaethler LB, Liu R, Lopez A, Nicorici A, Owens C, Rodriguez D, Wang J, Zhang H, Aranki D, McDonald CM, Henricson EK. PMID: 38400281; PMCID: PMC10892016.
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PubMed Mentions:
4 Fields:
Translation:
Humans
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Findings from the Longitudinal CINRG Becker Natural History Study. J Neuromuscul Dis. 2024; 11(1):201-212.
Clemens PR, Gordish-Dressman H, Niizawa G, Gorni K, Guglieri M, Connolly AM, Wicklund M, Bertorini T, Mah J, Thangarajh M, Smith EC, Kuntz NL, McDonald CM, Henricson E, Upadhyayula S, Byrne B, Manousakis G, Harper A, Iannaccone S, Dang UJ. PMID: 37980682; PMCID: PMC10789327.
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PubMed Mentions:
1 Fields:
Translation:
Humans
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Correction to: Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015-2022): 2022 interim analysis. J Neurol. 2023 Sep; 270(9):4583.
Mercuri E, Osorio AN, Muntoni F, Buccella F, Desguerre I, Kirschner J, Tulinius M, de Resende MBD, Morgenroth LP, Gordish-Dressman H, Johnson S, Kristensen A, Werner C, Trifillis P, Henricson EK, McDonald CM, STRIDE and CINRG DNHS investigators. PMID: 37460854; PMCID: PMC10421802.
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PubMed Mentions: Fields:
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Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015-2022): 2022 interim analysis. J Neurol. 2023 Aug; 270(8):3896-3913.
Mercuri E, Osorio AN, Muntoni F, Buccella F, Desguerre I, Kirschner J, Tulinius M, de Resende MBD, Morgenroth LP, Gordish-Dressman H, Johnson S, Kristensen A, Werner C, Trifillis P, Henricson EK, McDonald CM, STRIDE and CINRG DNHS investigators. PMID: 37115359; PMCID: PMC10141820.
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PubMed Mentions:
7 Fields:
Translation:
Humans
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Functional and Clinical Outcomes Associated with Steroid Treatment among Non-ambulatory Patients with Duchenne Muscular Dystrophy1. J Neuromuscul Dis. 2023; 10(1):67-79.
McDonald CM, Mayer OH, Hor KN, Miller D, Goemans N, Henricson EK, Marden JR, Freimark J, Lane H, Zhang A, Frean M, Trifillis P, Koladicz K, Signorovitch J, PRO-DMD-01 consortium investigators. PMID: 36565131; PMCID: PMC9881035.
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PubMed Mentions:
1 Fields:
Translation:
Humans
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Dystrophinopathy and the brain: A parent project muscular dystrophy (PPMD) meeting report November 11-12, 2021, New York City, NY. Neuromuscul Disord. 2022 Oct 20.
Colvin MK, Truba N, Sorensen S, Henricson E, Kinnett K, all participants. PMID: 36323606.
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PubMed Mentions:
1 Fields:
Translation:
Humans
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Delays in pulmonary decline in eteplirsen-treated patients with Duchenne muscular dystrophy. Muscle Nerve. 2022 09; 66(3):262-269.
Iff J, Gerrits C, Zhong Y, Tuttle E, Birk E, Zheng Y, Paul X, Henricson EK, McDonald CM, CINRG-DNHS Investigators. PMID: 35715998.
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PubMed Mentions:
5 Fields:
Translation:
Humans
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Longitudinal changes in cardiac function in Duchenne muscular dystrophy population as measured by magnetic resonance imaging. BMC Cardiovasc Disord. 2022 06 09; 22(1):260.
Batra A, Barnard AM, Lott DJ, Willcocks RJ, Forbes SC, Chakraborty S, Daniels MJ, Arbogast J, Triplett W, Henricson EK, Dayan JG, Schmalfuss C, Sweeney L, Byrne BJ, McDonald CM, Vandenborne K, Walter GA. PMID: 35681116; PMCID: PMC9185987.
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PubMed Mentions:
3 Fields:
Translation:
Humans
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Disease Progression Stages and Burden in Patients with Duchenne Muscular Dystrophy Using Administrative Claims Supplemented by Electronic Medical Records. Adv Ther. 2022 06; 39(6):2906-2919.
Iff J, Zhong Y, Gupta D, Paul X, Tuttle E, Henricson E, Schrader R, CINRG DNHS Investigators. PMID: 35460510.
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PubMed Mentions:
6 Fields:
Translation:
Humans
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Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial. JAMA. 2022 04 19; 327(15):1456-1468.
Guglieri M, Bushby K, McDermott MP, Hart KA, Tawil R, Martens WB, Herr BE, McColl E, Speed C, Wilkinson J, Kirschner J, King WM, Eagle M, Brown MW, Willis T, Griggs RC, FOR-DMD Investigators of the Muscle Study Group, Straub V, van Ruiten H, Childs AM, Ciafaloni E, Shieh PB, Spinty S, Maggi L, Baranello G, Butterfield RJ, Horrocks IA, Roper H, Alhaswani Z, Flanigan KM, Kuntz NL, Manzur A, Darras BT, Kang PB, Morrison L, Krzesniak-Swinarska M, Mah JK, Mongini TE, Ricci F, von der Hagen M, Finkel RS, O'Reardon K, Wicklund M, Kumar A, McDonald CM, Han JJ, Joyce N, Henricson EK, Schara-Schmidt U, Gangfuss A, Wilichowski E, Barohn RJ, Statland JM, Campbell C, Vita G, Vita GL, Howard JF, Hughes I, McMillan HJ, Pegoraro E, Bello L, Burnette WB, Thangarajh M, Chang T. PMID: 35381069; PMCID: PMC8984930.
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PubMed Mentions:
26 Fields:
Translation:
Humans
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Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial. Lancet. 2022 03 12; 399(10329):1049-1058.
McDonald CM, Marbán E, Hendrix S, Hogan N, Ruckdeschel Smith R, Eagle M, Finkel RS, Tian C, Janas J, Harmelink MM, Varadhachary AS, Taylor MD, Hor KN, Mayer OH, Henricson EK, Furlong P, Ascheim DD, Rogy S, Williams P, Marbán L, HOPE-2 Study Group. PMID: 35279258.
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PubMed Mentions:
19 Fields:
Translation:
HumansCTClinical Trials
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Knee Strength and Ankle Range of Motion Impacts on Timed Function Tests in Duchenne Muscular Dystrophy: In the Era of Glucocorticoids. J Neuromuscul Dis. 2022; 9(1):147-159.
Duong T, Canbek J, Fernandez-Fernandez A, Henricson E, Birkmeier M, Siener C, Tesi Rocha C, McDonald C, Gordish-Dressman H, CINRG Investigators. PMID: 34719507.
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PubMed Mentions:
2 Fields:
Translation:
Humans
-
Rasch Analysis of the Pediatric Quality of Life Inventory 4.0 Generic Core Scales Administered to Patients With Duchenne Muscular Dystrophy. Value Health. 2021 10; 24(10):1490-1498.
Landfeldt E, Iff J, Henricson E, Cooperative International Neuromuscular Research Group Investigators. PMID: 34593173; PMCID: PMC9132346.
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PubMed Mentions:
1 Fields:
Translation:
Humans
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The Minimal Clinical Important Difference (MCID) in Annual Rate of Change of Timed Function Tests in Boys with DMD. J Neuromuscul Dis. 2021; 8(6):939-948.
Duong T, Canbek J, Birkmeier M, Nelson L, Siener C, Fernandez-Fernandez A, Henricson E, McDonald CM, Gordish-Dressman H, CINRG-DNHS Investigators. PMID: 34151852; PMCID: PMC8673528.
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PubMed Mentions:
4 Fields:
Translation:
Humans
-
(-)-Epicatechin induces mitochondrial biogenesis and markers of muscle regeneration in adults with Becker muscular dystrophy. Muscle Nerve. 2021 02; 63(2):239-249.
McDonald CM, Ramirez-Sanchez I, Oskarsson B, Joyce N, Aguilar C, Nicorici A, Dayan J, Goude E, Abresch RT, Villarreal F, Ceballos G, Perkins G, Dugar S, Schreiner G, Henricson EK. PMID: 33125736; PMCID: PMC7898288.
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PubMed Mentions:
20 Fields:
Translation:
HumansCells
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The CINRG Becker Natural History Study: Baseline characteristics. Muscle Nerve. 2020 09; 62(3):369-376.
Clemens PR, Niizawa G, Feng J, Florence J, D'Alessandro AS, Morgenroth LP, Gorni K, Guglieri M, Connolly A, Wicklund M, Bertorini T, Mah JK, Thangarajh M, Smith E, Kuntz N, McDonald CM, Henricson EK, Upadhyayula S, Byrne B, Manousakis G, Harper A, Bravver E, Iannaccone S, Spurney C, Cnaan A, Gordish-Dressman H, CINRG BNHS Investigators. PMID: 32564389; PMCID: PMC7520226.
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PubMed Mentions:
10 Fields:
Translation:
Humans
-
Seven-Year Experience From the National Institute of Neurological Disorders and Stroke-Supported Network for Excellence in Neuroscience Clinical Trials. JAMA Neurol. 2020 06 01; 77(6):755-763.
Cudkowicz M, Chase MK, Coffey CS, Ecklund DJ, Thornell BJ, Lungu C, Mahoney K, Gutmann L, Shefner JM, Staley KJ, Bosch M, Foster E, Long JD, Bayman EO, Torner J, Yankey J, Peters R, Huff T, Conwit RA, NeuroNEXT Clinical Study Sites, Shinnar S, Patch D, Darras BT, Ellis A, Packer RJ, Marder KS, Chiriboga CA, Henchcliffe C, Moran JA, Nikolov B, Factor SA, Seeley C, Greenberg SM, Amato AA, DeGregorio S, Simuni T, Ward T, Kissel JT, Kolb SJ, Bartlett A, Quinn JF, Keith K, Levine SR, Gilles N, Coyle PK, Lamb J, Wolfe GI, Crumlish A, Mejico L, Iqbal MM, Bowen JD, Tongco C, Nabors LB, Bashir K, Benge M, McDonald CM, Henricson EK, Oskarsson B, Dobkin BH, Canamar C, Glauser TA, Woo D, Molloy A, Clark P, Vollmer TL, Stein AJ, Barohn RJ, Dimachkie MM, Le Pichon JB, Benatar MG, Steele J, Wechsler L, Clemens PR, Amity C, Holloway RG, Annis C, Goldberg MP, Andersen M, Iannaccone ST, Smith AG, Singleton JR, Doudova M, Haley EC, Quigg MS, Lowenhaupt S, Malow BA, Adkins K, Clifford DB, Teshome MA, Connolly N. PMID: 32202612; PMCID: PMC7483960.
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PubMed Mentions:
2 Fields:
Translation:
Humans
-
Identification and Analysis of Bacterial Contamination of Ultrasound Transducers and Multiuse Ultrasound Transmission Gel Bottle Tips Before and After the Aseptic Cleansing Technique. J Ultrasound Med. 2020 Oct; 39(10):1957-1963.
Mullins K, Burnham K, Henricson EK, Cohen S, Fair J, Ray JW. PMID: 32339352.
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PubMed Mentions:
3 Fields:
Translation:
HumansCellsPHPublic Health
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Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study. J Comp Eff Res. 2020 04; 9(5):341-360.
Mercuri E, Muntoni F, Osorio AN, Tulinius M, Buccella F, Morgenroth LP, Gordish-Dressman H, Jiang J, Trifillis P, Zhu J, Kristensen A, Santos CL, Henricson EK, McDonald CM, Desguerre I, STRIDE, CINRG Duchenne Natural History Investigators. PMID: 31997646; PMCID: PMC7610147.
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PubMed Mentions:
39 Fields:
Translation:
Humans
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Disease-specific and glucocorticoid-responsive serum biomarkers for Duchenne Muscular Dystrophy. Sci Rep. 2019 08 21; 9(1):12167.
Hathout Y, Liang C, Ogundele M, Xu G, Tawalbeh SM, Dang UJ, Hoffman EP, Gordish-Dressman H, Conklin LS, van den Anker JN, Clemens PR, Mah JK, Henricson E, McDonald C. PMID: 31434957; PMCID: PMC6704115.
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PubMed Mentions:
24 Fields:
Translation:
Humans
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Towards regulatory endorsement of drug development tools to promote the application of model-informed drug development in Duchenne muscular dystrophy. J Pharmacokinet Pharmacodyn. 2019 10; 46(5):441-455.
Conrado DJ, Larkindale J, Berg A, Hill M, Burton J, Abrams KR, Abresch RT, Bronson A, Chapman D, Crowther M, Duong T, Gordish-Dressman H, Harnisch L, Henricson E, Kim S, McDonald CM, Schmidt S, Vong C, Wang X, Wong BL, Yong F, Romero K, Duchenne Muscular Dystrophy Regulatory Science Consortium (D-RSC). PMID: 31127458.
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PubMed Mentions:
10 Fields:
Translation:
Humans
-
Eteplirsen Treatment Attenuates Respiratory Decline in Ambulatory and Non-Ambulatory Patients with Duchenne Muscular Dystrophy. J Neuromuscul Dis. 2019; 6(2):213-225.
Khan N, Eliopoulos H, Han L, Kinane TB, Lowes LP, Mendell JR, Gordish-Dressman H, Henricson EK, McDonald CM, Eteplirsen Investigators and the CINRG DNHS Investigators. PMID: 30856119; PMCID: PMC6598025.
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PubMed Mentions:
39 Fields:
Translation:
Humans
-
Neurodevelopmental Needs in Young Boys with Duchenne Muscular Dystrophy (DMD): Observations from the Cooperative International Neuromuscular Research Group (CINRG) DMD Natural History Study (DNHS). PLoS Curr. 2018 10 17; 10.
Thangarajh M, Spurney CF, Gordish-Dressman H, Clemens PR, Hoffman EP, McDonald CM, Henricson EK, CINRG Investigators. PMID: 30443431; PMCID: PMC6209412.
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PubMed Mentions:
7
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Longitudinal pulmonary function testing outcome measures in Duchenne muscular dystrophy: Long-term natural history with and without glucocorticoids. Neuromuscul Disord. 2018 11; 28(11):897-909.
McDonald CM, Gordish-Dressman H, Henricson EK, Duong T, Joyce NC, Jhawar S, Leinonen M, Hsu F, Connolly AM, Cnaan A, Abresch RT, CINRG investigators for PubMed. PMID: 30336970.
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PubMed Mentions:
43 Fields:
Translation:
Humans
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Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study. Lancet. 2018 02 03; 391(10119):451-461.
McDonald CM, Henricson EK, Abresch RT, Duong T, Joyce NC, Hu F, Clemens PR, Hoffman EP, Cnaan A, Gordish-Dressman H, CINRG Investigators. PMID: 29174484.
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PubMed Mentions:
182 Fields:
Translation:
HumansCTClinical Trials
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Interleukin 1 Receptor-Like 1 Protein (ST2) is a Potential Biomarker for Cardiomyopathy in Duchenne Muscular Dystrophy. Pediatr Cardiol. 2017 Dec; 38(8):1606-1612.
Anderson J, Seol H, Gordish-Dressman H, Hathout Y, Spurney CF, CINRG Investigators. PMID: 28821969; PMCID: PMC6317901.
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PubMed Mentions:
10 Fields:
Translation:
Humans
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Pulmonary Endpoints in Duchenne Muscular Dystrophy. A Workshop Summary. Am J Respir Crit Care Med. 2017 08 15; 196(4):512-519.
Finder J, Mayer OH, Sheehan D, Sawnani H, Abresch RT, Benditt J, Birnkrant DJ, Duong T, Henricson E, Kinnett K, McDonald CM, Connolly AM. PMID: 28636407.
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PubMed Mentions:
15 Fields:
Translation:
Humans
-
Duchenne Regulatory Science Consortium Meeting on Disease Progression Modeling for Duchenne Muscular Dystrophy. PLoS Curr. 2017 Jan 12; 9.
Larkindale J, Abresch R, Aviles E, Bronson A, Chin J, Furlong P, Gordish-Dressman H, Habeeb-Louks E, Henricson E, Kroger H, Lynn C, Lynn S, Martin D, Nuckolls G, Rooney W, Romero K, Sweeney L, Vandenborne K, Walter G, Wolff J, Wong B, McDonald CM, Duchenne Regulatory Science Consortium Imaging-Dmd Consortium And The Cinrg Investigators MO. PMID: 28228973; PMCID: PMC5300692.
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PubMed Mentions:
4
-
Characterization of pulmonary function in 10-18 year old patients with Duchenne muscular dystrophy. Neuromuscul Disord. 2017 Apr; 27(4):307-314.
Meier T, Rummey C, Leinonen M, Spagnolo P, Mayer OH, Buyse GM, DELOS Study Group. PMID: 28189481.
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PubMed Mentions:
14 Fields:
Translation:
Humans
-
Advances in Pulmonary Care in Duchenne Muscular Dystrophy. US Neurology. 2017 Jan 1; 13(01):35.
Mayer MO, Henricson HE, McDonald MC, Buyse BG. .
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Publisher Site Mentions:
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Association Study of Exon Variants in the NF-κB and TGFβ Pathways Identifies CD40 as a Modifier of Duchenne Muscular Dystrophy. Am J Hum Genet. 2016 Nov 03; 99(5):1163-1171.
Bello L, Flanigan KM, Weiss RB, United Dystrophinopathy Project, Spitali P, Aartsma-Rus A, Muntoni F, Zaharieva I, Ferlini A, Mercuri E, Tuffery-Giraud S, Claustres M, Straub V, Lochmüller H, Barp A, Vianello S, Pegoraro E, Punetha J, Gordish-Dressman H, Giri M, McDonald CM, Hoffman EP, Cooperative International Neuromuscular Research Group. PMID: 27745838; PMCID: PMC5097949.
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PubMed Mentions:
41 Fields:
Translation:
Humans
-
Development of a patient-reported outcome measure for upper limb function in Duchenne muscular dystrophy: DMD Upper Limb PROM. Dev Med Child Neurol. 2017 Feb; 59(2):224-231.
Klingels K, Mayhew AG, Mazzone ES, Duong T, Decostre V, Werlauff U, Vroom E, Mercuri E, Goemans NM, Upper Limb Clinical Outcome Group. PMID: 27671699.
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PubMed Mentions:
17 Fields:
Translation:
Humans
-
Serum pharmacodynamic biomarkers for chronic corticosteroid treatment of children. Sci Rep. 2016 08 17; 6:31727.
Hathout Y, Conklin LS, Seol H, Gordish-Dressman H, Brown KJ, Morgenroth LP, Nagaraju K, Heier CR, Damsker JM, van den Anker JN, Henricson E, Clemens PR, Mah JK, McDonald C, Hoffman EP. PMID: 27530235; PMCID: PMC4987691.
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PubMed Mentions:
27 Fields:
Translation:
Humans
-
Correction: Discovery of Metabolic Biomarkers for Duchenne Muscular Dystrophy within a Natural History Study. PLoS One. 2016; 11(7):e0159895.
Boca SM, Nishida M, Harris M, Rao S, Cheema AK, Gill K, Wang D, An L, Gauba R, Seol H, Morgenroth LP, Henricson E, McDonald C, Mah JK, Clemens PR, Hoffman EP, Hathout Y, Madhavan S. PMID: 27434074; PMCID: PMC4951084.
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PubMed Mentions:
7 Fields:
-
Discovery of Metabolic Biomarkers for Duchenne Muscular Dystrophy within a Natural History Study. PLoS One. 2016; 11(4):e0153461.
Boca SM, Nishida M, Harris M, Rao S, Cheema AK, Gill K, Seol H, Morgenroth LP, Henricson E, McDonald C, Mah JK, Clemens PR, Hoffman EP, Hathout Y, Madhavan S. PMID: 27082433; PMCID: PMC4833348.
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PubMed Mentions:
17 Fields:
Translation:
Humans
-
Prednisone/prednisolone and deflazacort regimens in the CINRG Duchenne Natural History Study. Neurology. 2015 Sep 22; 85(12):1048-55.
Bello L, Gordish-Dressman H, Morgenroth LP, Henricson EK, Duong T, Hoffman EP, Cnaan A, McDonald CM, CINRG Investigators. PMID: 26311750; PMCID: PMC4603595.
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PubMed Mentions:
93 Fields:
Translation:
Humans
-
Large-scale serum protein biomarker discovery in Duchenne muscular dystrophy. Proc Natl Acad Sci U S A. 2015 Jun 09; 112(23):7153-8.
Hathout Y, Brody E, Clemens PR, Cripe L, DeLisle RK, Furlong P, Gordish-Dressman H, Hache L, Henricson E, Hoffman EP, Kobayashi YM, Lorts A, Mah JK, McDonald C, Mehler B, Nelson S, Nikrad M, Singer B, Steele F, Sterling D, Sweeney HL, Williams S, Gold L. PMID: 26039989; PMCID: PMC4466703.
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PubMed Mentions:
154 Fields:
Translation:
Humans
-
Genetic modifiers of ambulation in the Cooperative International Neuromuscular Research Group Duchenne Natural History Study. Ann Neurol. 2015 Apr; 77(4):684-96.
Bello L, Kesari A, Gordish-Dressman H, Cnaan A, Morgenroth LP, Punetha J, Duong T, Henricson EK, Pegoraro E, McDonald CM, Hoffman EP, Cooperative International Neuromuscular Research Group Investigators. PMID: 25641372; PMCID: PMC4403971.
View in:
PubMed Mentions:
72 Fields:
Translation:
Humans
-
Ataluren treatment of patients with nonsense mutation dystrophinopathy. Muscle Nerve. 2014 Oct; 50(4):477-87.
Bushby K, Finkel R, Wong B, Barohn R, Campbell C, Comi GP, Connolly AM, Day JW, Flanigan KM, Goemans N, Jones KJ, Mercuri E, Quinlivan R, Renfroe JB, Russman B, Ryan MM, Tulinius M, Voit T, Moore SA, Lee Sweeney H, Abresch RT, Coleman KL, Eagle M, Florence J, Gappmaier E, Glanzman AM, Henricson E, Barth J, Elfring GL, Reha A, Spiegel RJ, O'donnell MW, Peltz SW, Mcdonald CM, PTC124-GD-007-DMD STUDY GROUP. PMID: 25042182; PMCID: PMC4241581.
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PubMed Mentions:
179 Fields:
Translation:
Humans
-
Discovery of serum protein biomarkers in the mdx mouse model and cross-species comparison to Duchenne muscular dystrophy patients. Hum Mol Genet. 2014 Dec 15; 23(24):6458-69.
Hathout Y, Marathi RL, Rayavarapu S, Zhang A, Brown KJ, Seol H, Gordish-Dressman H, Cirak S, Bello L, Nagaraju K, Partridge T, Hoffman EP, Takeda S, Mah JK, Henricson E, McDonald C. PMID: 25027324; PMCID: PMC4240201.
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PubMed Mentions:
69 Fields:
Translation:
HumansAnimals
-
Development of the Performance of the Upper Limb module for Duchenne muscular dystrophy. Dev Med Child Neurol. 2013 Nov; 55(11):1038-45.
Mayhew A, Mazzone ES, Eagle M, Duong T, Ash M, Decostre V, Vandenhauwe M, Klingels K, Florence J, Main M, Bianco F, Henrikson E, Servais L, Campion G, Vroom E, Ricotti V, Goemans N, McDonald C, Mercuri E, Performance of the Upper Limb Working Group. PMID: 23902233.
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PubMed Mentions:
81 Fields:
Translation:
Humans
-
The 6-minute walk test and other clinical endpoints in duchenne muscular dystrophy: reliability, concurrent validity, and minimal clinically important differences from a multicenter study. Muscle Nerve. 2013 Sep; 48(3):357-68.
McDonald CM, Henricson EK, Abresch RT, Florence J, Eagle M, Gappmaier E, Glanzman AM, PTC124-GD-007-DMD Study Group, Spiegel R, Barth J, Elfring G, Reha A, Peltz SW. PMID: 23674289; PMCID: PMC3826053.
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PubMed Mentions:
124 Fields:
Translation:
Humans
-
The 6-Minute Walk Test and Person-Reported Outcomes in Boys with Duchenne Muscular Dystrophy and Typically Developing Controls: Longitudinal Comparisons and Clinically-Meaningful Changes Over One Year. PLoS Curr. 2013 Jul 08; 5.
Henricson E, Abresch R, Han JJ, Nicorici A, Goude Keller E, de Bie E, McDonald CM. PMID: 23867975.
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PubMed Mentions:
53
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The 6-minute walk test and other endpoints in Duchenne muscular dystrophy: longitudinal natural history observations over 48 weeks from a multicenter study. Muscle Nerve. 2013 Sep; 48(3):343-56.
McDonald CM, Henricson EK, Abresch RT, Florence JM, Eagle M, Gappmaier E, Glanzman AM, PTC124-GD-007-DMD Study Group, Spiegel R, Barth J, Elfring G, Reha A, Peltz S. PMID: 23681930; PMCID: PMC3824082.
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PubMed Mentions:
133 Fields:
Translation:
Humans
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The cooperative international neuromuscular research group Duchenne natural history study--a longitudinal investigation in the era of glucocorticoid therapy: design of protocol and the methods used. Muscle Nerve. 2013 Jul; 48(1):32-54.
McDonald CM, Henricson EK, Abresch RT, Han JJ, Escolar DM, Florence JM, Duong T, Arrieta A, Clemens PR, Hoffman EP, Cnaan A, Cinrg Investigators. PMID: 23677550; PMCID: PMC4147958.
View in:
PubMed Mentions:
89 Fields:
Translation:
Humans
-
The cooperative international neuromuscular research group Duchenne natural history study: glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing and other commonly used clinical trial outcome measures. Muscle Nerve. 2013 Jul; 48(1):55-67.
Henricson EK, Abresch RT, Cnaan A, Hu F, Duong T, Arrieta A, Han J, Escolar DM, Florence JM, Clemens PR, Hoffman EP, McDonald CM, CINRG Investigators. PMID: 23649481; PMCID: PMC4103170.
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PubMed Mentions:
95 Fields:
Translation:
Humans
-
Energy expenditure estimation with smartphone body sensors. . 2013 Jan 1; 8-14.
Pande PA, Zeng ZY, Das DA, Mohapatra MP, Miyamoto MS, Seto SE, Henricson HE, Han HJ. .
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Publisher Site Mentions:
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Randomized controlled trial comparing acupuncture with placebo acupuncture for the treatment of carpal tunnel syndrome. PM R. 2012 May; 4(5):367-73.
Yao E, Gerritz PK, Henricson E, Abresch T, Kim J, Han J, Wang K, Zhao H. PMID: 22405683.
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PubMed Mentions:
16 Fields:
Translation:
Humans
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Pentoxifylline as a rescue treatment for DMD: a randomized double-blind clinical trial. Neurology. 2012 Mar 20; 78(12):904-13.
Escolar DM, Zimmerman A, Bertorini T, Clemens PR, Connolly AM, Mesa L, Gorni K, Kornberg A, Kolski H, Kuntz N, Nevo Y, Tesi-Rocha C, Nagaraju K, Rayavarapu S, Hache LP, Mayhew JE, Florence J, Hu F, Arrieta A, Henricson E, Leshner RT, Mah JK. PMID: 22402864; PMCID: PMC3306159.
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PubMed Mentions:
16 Fields:
Translation:
Humans
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Percent-predicted 6-minute walk distance in duchenne muscular dystrophy to account for maturational influences. PLoS Curr. 2012 Jan 25; 3:RRN1297.
Henricson E, Abresch R, Han JJ, Nicorici A, Goude Keller E, Elfring G, Reha A, Barth J, McDonald CM. PMID: 22306689; PMCID: PMC3269886.1.
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PubMed Mentions:
31
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Quality-of-life measures in children with neurological conditions: pediatric Neuro-QOL. Neurorehabil Neural Repair. 2012 Jan; 26(1):36-47.
Lai JS, Nowinski C, Victorson D, Bode R, Podrabsky T, McKinney N, Straube D, Holmes GL, McDonald CM, Henricson E, Abresch RT, Moy CS, Cella D. PMID: 21788436; PMCID: PMC3710728.
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PubMed Mentions:
35 Fields:
Translation:
Humans
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Randomized, blinded trial of weekend vs daily prednisone in Duchenne muscular dystrophy. Neurology. 2011 Aug 02; 77(5):444-52.
Escolar DM, Hache LP, Clemens PR, Cnaan A, McDonald CM, Viswanathan V, Kornberg AJ, Bertorini TE, Nevo Y, Lotze T, Pestronk A, Ryan MM, Monasterio E, Day JW, Zimmerman A, Arrieta A, Henricson E, Mayhew J, Florence J, Hu F, Connolly AM. PMID: 21753160; PMCID: PMC3146308.
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PubMed Mentions:
69 Fields:
Translation:
Humans
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CINRG pilot trial of coenzyme Q10 in steroid-treated Duchenne muscular dystrophy. Muscle Nerve. 2011 Aug; 44(2):174-8.
Spurney CF, Rocha CT, Henricson E, Florence J, Mayhew J, Gorni K, Pasquali L, Pestronk A, Martin GR, Hu F, Nie L, Connolly AM, Escolar DM, Cooperative International Neuromuscular Research Group Investigators. PMID: 21698649; PMCID: PMC3136634.
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PubMed Mentions:
21 Fields:
Translation:
HumansCTClinical Trials
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Liquid formulation of pentoxifylline is a poorly tolerated treatment for duchenne dystrophy. Muscle Nerve. 2011 Aug; 44(2):170-3.
Zimmerman A, Clemens PR, Tesi-Rocha C, Connolly A, Iannaccone ST, Kuntz N, Arrieta A, Hache L, Henricson E, Hu F, Mayhew J, Escolar DM. PMID: 21674534; PMCID: PMC3136640.
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PubMed Mentions:
4 Fields:
Translation:
HumansCTClinical Trials
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The 6-minute walk test in Duchenne/Becker muscular dystrophy: longitudinal observations. Muscle Nerve. 2010 Dec; 42(6):966-74.
McDonald CM, Henricson EK, Han JJ, Abresch RT, Nicorici A, Atkinson L, Elfring GL, Reha A, Miller LL. PMID: 21038378.
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PubMed Mentions:
65 Fields:
Translation:
Humans
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Relationship between clinical outcome measures and parent proxy reports of health-related quality of life in ambulatory children with Duchenne muscular dystrophy. J Child Neurol. 2010 Sep; 25(9):1130-44.
McDonald CM, McDonald DA, Bagley A, Sienko Thomas S, Buckon CE, Henricson E, Nicorici A, Sussman MD. PMID: 20558672; PMCID: PMC3695468.
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PubMed Mentions:
25 Fields:
Translation:
Humans
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The 6-minute walk test as a new outcome measure in Duchenne muscular dystrophy. Muscle Nerve. 2010 Apr; 41(4):500-10.
McDonald CM, Henricson EK, Han JJ, Abresch RT, Nicorici A, Elfring GL, Atkinson L, Reha A, Hirawat S, Miller LL. PMID: 19941337.
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PubMed Mentions:
138 Fields:
Translation:
Humans
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CINRG pilot trial of oxatomide in steroid-naïve Duchenne muscular dystrophy. Eur J Paediatr Neurol. 2007 Nov; 11(6):337-40.
Buyse GM, Goemans N, Henricson E, Jara A, van den Hauwe M, Leshner R, Florence JM, Mayhew JE, Escolar DM. PMID: 17459739.
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PubMed Mentions:
7 Fields:
Translation:
Humans
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Reliable surrogate outcome measures in multicenter clinical trials of Duchenne muscular dystrophy. Muscle Nerve. 2007 Jan; 35(1):36-42.
Mayhew JE, Florence JM, Mayhew TP, Henricson EK, Leshner RT, McCarter RJ, Escolar DM. PMID: 16969838.
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PubMed Mentions:
47 Fields:
Translation:
HumansCTClinical Trials
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CINRG randomized controlled trial of creatine and glutamine in Duchenne muscular dystrophy. Ann Neurol. 2005 Jul; 58(1):151-5.
Escolar DM, Buyse G, Henricson E, Leshner R, Florence J, Mayhew J, Tesi-Rocha C, Gorni K, Pasquali L, Patel KM, McCarter R, Huang J, Mayhew T, Bertorini T, Carlo J, Connolly AM, Clemens PR, Goemans N, Iannaccone ST, Igarashi M, Nevo Y, Pestronk A, Subramony SH, Vedanarayanan VV, Wessel H, CINRG Group. PMID: 15984021.
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PubMed Mentions:
31 Fields:
Translation:
HumansCTClinical Trials
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Collaborative translational research leading to multicenter clinical trials in Duchenne muscular dystrophy: the Cooperative International Neuromuscular Research Group (CINRG). Neuromuscul Disord. 2002 Oct; 12 Suppl 1:S147-154.
Escolar DM, Henricson EK, Pasquali L, Gorni K, Hoffman EP. PMID: 12206809.
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PubMed Mentions:
5 Fields:
Translation:
HumansAnimals
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Clinical evaluator reliability for quantitative and manual muscle testing measures of strength in children. Muscle Nerve. 2001 Jun; 24(6):787-93.
Escolar DM, Henricson EK, Mayhew J, Florence J, Leshner R, Patel KM, Clemens PR. PMID: 11360262.
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PubMed Mentions:
52 Fields:
Translation:
Humans